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Fragile X Syndrome - Pipeline Review, H2 2017

Published: Sep, 2017 | Pages: 121 | Publisher: Global Markets Direct
Industry: Pharmaceuticals & Healthcare | Report Format: Electronic (PDF)

Fragile X Syndrome - Pipeline Review, H2 2017

Summary

Global Markets Direct's latest Pharmaceutical and Healthcare disease pipeline guide Fragile X Syndrome - Pipeline Review, H2 2017, provides an overview of the Fragile X Syndrome (Genetic Disorders) pipeline landscape.

Fragile X syndrome is a genetic condition that causes a range of developmental problems including learning disabilities and cognitive impairment. Fragile X syndrome is caused by a change in a gene called FMR1. Fragile X syndrome occurs both in male and female. Symptoms include delay in crawling, walking, or twisting, hyperactive or impulsive behavior, speech and language delay and intellectual disability. 

Report Highlights

Global Markets Direct's Pharmaceutical and Healthcare latest pipeline guide Fragile X Syndrome - Pipeline Review, H2 2017, provides comprehensive information on the therapeutics under development for Fragile X Syndrome (Genetic Disorders), complete with analysis by stage of development, drug target, mechanism of action (MoA), route of administration (RoA) and molecule type. The guide covers the descriptive pharmacological action of the therapeutics, its complete research and development history and latest news and press releases.

The Fragile X Syndrome (Genetic Disorders) pipeline guide also reviews of key players involved in therapeutic development for Fragile X Syndrome and features dormant and discontinued projects. The guide covers therapeutics under Development by Companies /Universities /Institutes, the molecules developed by Companies in Phase III, Phase II, Phase I, Preclinical and Discovery stages are 1, 3, 4, 14 and 1 respectively. Similarly, the Universities portfolio in Preclinical and Discovery stages comprises 3 and 2 molecules, respectively.

Fragile X Syndrome (Genetic Disorders) pipeline guide helps in identifying and tracking emerging players in the market and their portfolios, enhances decision making capabilities and helps to create effective counter strategies to gain competitive advantage. The guide is built using data and information sourced from Global Markets Direct's proprietary databases, company/university websites, clinical trial registries, conferences, SEC filings, investor presentations and featured press releases from company/university sites and industry-specific third party sources. Additionally, various dynamic tracking processes ensure that the most recent developments are captured on a real time basis.

Note: Certain content / sections in the pipeline guide may be removed or altered based on the availability and relevance of data.

Scope

- The pipeline guide provides a snapshot of the global therapeutic landscape of Fragile X Syndrome (Genetic Disorders).
- The pipeline guide reviews pipeline therapeutics for Fragile X Syndrome (Genetic Disorders) by companies and universities/research institutes based on information derived from company and industry-specific sources. 
- The pipeline guide covers pipeline products based on several stages of development ranging from pre-registration till discovery and undisclosed stages.
- The pipeline guide features descriptive drug profiles for the pipeline products which comprise, product description, descriptive licensing and collaboration details, R&D brief, MoA & other developmental activities.
- The pipeline guide reviews key companies involved in Fragile X Syndrome (Genetic Disorders) therapeutics and enlists all their major and minor projects.
- The pipeline guide evaluates Fragile X Syndrome (Genetic Disorders) therapeutics based on mechanism of action (MoA), drug target, route of administration (RoA) and molecule type.
- The pipeline guide encapsulates all the dormant and discontinued pipeline projects. 
- The pipeline guide reviews latest news related to pipeline therapeutics for Fragile X Syndrome (Genetic Disorders)

Reasons To Buy

- Procure strategically important competitor information, analysis, and insights to formulate effective R&D strategies.
- Recognize emerging players with potentially strong product portfolio and create effective counter-strategies to gain competitive advantage.
- Find and recognize significant and varied types of therapeutics under development for Fragile X Syndrome (Genetic Disorders).
- Classify potential new clients or partners in the target demographic.
- Develop tactical initiatives by understanding the focus areas of leading companies.
- Plan mergers and acquisitions meritoriously by identifying key players and it's most promising pipeline therapeutics.
- Formulate corrective measures for pipeline projects by understanding Fragile X Syndrome (Genetic Disorders) pipeline depth and focus of Indication therapeutics.
- Develop and design in-licensing and out-licensing strategies by identifying prospective partners with the most attractive projects to enhance and expand business potential and scope.
- Adjust the therapeutic portfolio by recognizing discontinued projects and understand from the know-how what drove them from pipeline.
 Table of Contents
Table of Contents 2 List of Tables 4 List of Figures 4 Introduction 5 Global Markets Direct Report Coverage 5 Fragile X Syndrome - Overview 6 Fragile X Syndrome - Therapeutics Development 7 Pipeline Overview 7 Pipeline by Companies 8 Pipeline by Universities/Institutes 11 Products under Development by Companies 12 Products under Development by Universities/Institutes 14 Fragile X Syndrome - Therapeutics Assessment 15 Assessment by Target 15 Assessment by Mechanism of Action 18 Assessment by Route of Administration 21 Assessment by Molecule Type 23 Fragile X Syndrome - Companies Involved in Therapeutics Development 25 Aelis Farma SAS 25 AMO Pharma Ltd 25 Anavex Life Sciences Corp 25 Confluence Pharmaceuticals LLC 26 DRI Biosciences Corp 26 Eli Lilly and Company 26 Fulcrum Therapeutics Inc 27 GlaxoSmithKline Plc 27 GW Pharmaceuticals Plc 28 Marinus Pharmaceuticals Inc 28 Neuren Pharmaceuticals Ltd 29 Neuron Biopharma SA 29 Ovid Therapeutics Inc 30 Sage Therapeutics Inc 30 Sentinel Oncology Ltd 31 Zynerba Pharmaceuticals Inc 31 Fragile X Syndrome - Drug Profiles 32 acamprosate calcium - Drug Profile 32 ACT-01 - Drug Profile 33 AMO-01 - Drug Profile 34 ANAVEX-273 - Drug Profile 36 AUT-00206 - Drug Profile 46 Bryostatin-1 - Drug Profile 48 cannabidiol - Drug Profile 54 cercosporamide - Drug Profile 64 Drug to Antagonize mGluR5 for Fragile X Syndrome and 16p11.2 Microdeletion Syndrome - Drug Profile 65 flindokalner - Drug Profile 66 gaboxadol - Drug Profile 67 ganaxolone - Drug Profile 70 GWP-42006 - Drug Profile 78 JRP-655 - Drug Profile 80 NNZ-2591 - Drug Profile 81 NST-0076 - Drug Profile 83 SAGE-217 - Drug Profile 84 SERx-519 - Drug Profile 88 SGE-872 - Drug Profile 89 Small Molecule for Fragile X-Associated Tremor Ataxia Syndrome - Drug Profile 90 Small Molecule to Activate FMRP for Fragile X Syndrome - Drug Profile 91 Small Molecule to Antagonize CB1R for Fragile X Syndrome and Down Syndrome - Drug Profile 92 Small Molecule to Block Kv3.1 for Fragile X Syndrome - Drug Profile 93 Small Molecules to Activate Slack Channels for Fragile X Syndrome - Drug Profile 94 Small Molecules to Inhibit PI3K for Autism and Fragile X Syndrome - Drug Profile 95 SOL-101 - Drug Profile 96 TC-2153 - Drug Profile 97 trofinetide - Drug Profile 98 Fragile X Syndrome - Dormant Projects 106 Fragile X Syndrome - Discontinued Products 108 Fragile X Syndrome - Product Development Milestones 109 Featured News & Press Releases 109 Appendix 118 Methodology 118 Coverage 118 Secondary Research 118 Primary Research 118 Expert Panel Validation 118 Contact Us 118 Disclaimer 119
List of Tables
Number of Products under Development for Fragile X Syndrome, H2 2017 Number of Products under Development by Companies, H2 2017 Number of Products under Development by Companies, H2 2017 (Contd..1), H2 2017 Number of Products under Development by Universities/Institutes, H2 2017 Products under Development by Companies, H2 2017 Products under Development by Companies, H2 2017 (Contd..1), H2 2017 Products under Development by Universities/Institutes, H2 2017 Number of Products by Stage and Target, H2 2017 Number of Products by Stage and Target, H2 2017 (Contd..1), H2 2017 Number of Products by Stage and Mechanism of Action, H2 2017 Number of Products by Stage and Mechanism of Action, H2 2017 (Contd..1), H2 2017 Number of Products by Stage and Route of Administration, H2 2017 Number of Products by Stage and Molecule Type, H2 2017 Fragile X Syndrome - Pipeline by Aelis Farma SAS, H2 2017 Fragile X Syndrome - Pipeline by AMO Pharma Ltd, H2 2017 Fragile X Syndrome - Pipeline by Anavex Life Sciences Corp, H2 2017 Fragile X Syndrome - Pipeline by Confluence Pharmaceuticals LLC, H2 2017 Fragile X Syndrome - Pipeline by DRI Biosciences Corp, H2 2017 Fragile X Syndrome - Pipeline by Eli Lilly and Company, H2 2017 Fragile X Syndrome - Pipeline by Fulcrum Therapeutics Inc, H2 2017 Fragile X Syndrome - Pipeline by GlaxoSmithKline Plc, H2 2017 Fragile X Syndrome - Pipeline by GW Pharmaceuticals Plc, H2 2017 Fragile X Syndrome - Pipeline by Marinus Pharmaceuticals Inc, H2 2017 Fragile X Syndrome - Pipeline by Neuren Pharmaceuticals Ltd, H2 2017 Fragile X Syndrome - Pipeline by Neuron Biopharma SA, H2 2017 Fragile X Syndrome - Pipeline by Ovid Therapeutics Inc, H2 2017 Fragile X Syndrome - Pipeline by Sage Therapeutics Inc, H2 2017 Fragile X Syndrome - Pipeline by Sentinel Oncology Ltd, H2 2017 Fragile X Syndrome - Pipeline by Zynerba Pharmaceuticals Inc, H2 2017 Fragile X Syndrome - Dormant Projects, H2 2017 Fragile X Syndrome - Dormant Projects, H2 2017 (Contd..1), H2 2017 Fragile X Syndrome - Discontinued Products, H2 2017



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